In December, 2016 experts from around the globe convened in London for the International Conference for Cognitive Endpoints in MPS. A consensus panel, led by Dr. Hanneke van der Lee, met to address cognitive endpoints in MPS I, MPS II and MPS III. The resulting literature review and paper now are published and are open access.
Cognitive and adaptive measurement endpoints for clinical trials in mucopolysaccharidoses types I, II, and III: A review of the literature:
Cognitive endpoints for therapy development for neuronopathic mucopolysaccharidoses: Results of a consensus procedure:
Thank you to the National MPS Society, the MPS Society of the UK and to all our our industry partners for support in making this endevour possible.